









Debra Litwak
Senior Director, Global Medical Affairs - Investigator Initiated Trials & Expanded Access Programs
BeOne Medicines






Rafael Escandon
Pediatric Gene Therapy Medical Ethics Working Group (PGTME)
NYU Grossman School of Medicine




Senior Director, Global Medical Affairs - Investigator Initiated Trials & Expanded Access Programs
BeOne Medicines
Pediatric Gene Therapy Medical Ethics Working Group (PGTME)
NYU Grossman School of Medicine